Curt Oltmans
Fulcrum Therapeutic
Del Lebel
Alexion, AstraZeneca Rare Disease
Kathy Perez
argenx
Chris Porter
Travere Therapeutics
Max Bronstein
Crinetics Pharmaceuticals
Dianne Berry
Sarepta Therapeutics
Molly Cameron,
Marinus Pharmaceuticals
Gina Cioffi,
Chiesi Global Rare Diseases
Katie Jones
Alexion, AstraZeneca Rare Disease
Kate Segal
Sarepta Therapeutics
Ken Sprague,
BioMarin